Rare Disease Trial Updates: October 2026
In October 2026, Trial Friend tracked 654 rare disease clinical trial updates across 130 conditions, including 1 FDA-related actions and 88 trial status changes, alongside enrollment updates and new trial site openings sourced from ClinicalTrials.gov and FDA announcements.
This is a permanent monthly archive. For the latest updates, see the live current events feed.
Major Updates: FDA Actions, Status Changes & Results
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
Now recruiting (was Active Not Recruiting)
The U.S. Food and Drug Administration today granted accelerated approval for Voceryq (doruxapapogene ralaplasmid and lalikinogene sifuplasmid-gxfd) for treatment of adults with recurrent respiratory papillomatosis (RRP).
No longer enrolling new participants
No longer enrolling new participants
Now recruiting (was Enrolling By Invitation)
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
Now recruiting (was Active Not Recruiting)
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
Now recruiting (was Active Not Recruiting)
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
Now recruiting (was Active Not Recruiting)
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
Now recruiting (was Active Not Recruiting)
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
Status changed from Recruiting to Enrolling By Invitation
No longer enrolling new participants
No longer enrolling new participants
Now recruiting (was Active Not Recruiting)
Now recruiting (was Enrolling By Invitation)
Status changed from Recruiting to Enrolling By Invitation
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
Now recruiting (was Active Not Recruiting)
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
No longer enrolling new participants
Trial Site & Enrollment Activity
Added 1 new site: Chapel Hill, North Carolina
Added 9 new sites: O'Fallon, Illinois, O'Fallon, Illinois, City of Saint Peters, Missouri and 6 more
Added 1 new site: Houston, Texas
Added 1 new site: Minneapolis, Minnesota
Added 4 new sites: Tampa, Florida, Stony Brook, New York, Oklahoma City, Oklahoma and 1 more
Added 1 new site: Madison, Wisconsin
Added 3 new sites: Ocoee, Florida, Durham, North Carolina, St Leonards, Australia
Added 3 new sites: Birmingham, Alabama, Fort Collins, Colorado, Savannah, Georgia
Added 1 new site: Atlanta, Georgia
Target enrollment decreased from 600 to 240
Eligibility criteria have been updated
Added 3 new sites: Barcelona, Spain, Santander, Spain, Seville, Spain
Reduced from 58 to 51 sites
Eligibility criteria have been updated
Eligibility criteria have been updated
Added 2 new sites: Knoxville, Tennessee, Tel HaShomer, Israel
Eligibility criteria have been updated
Added 1 new site: Buffalo, New York
Added 18 new sites: Beijing, China, Beijing, China, Chongqing, China and 15 more
Eligibility criteria have been updated
Eligibility criteria have been updated
Eligibility criteria have been updated
Added 1 new site: Marseille, France
Added 2 new sites: São Paulo, Brazil, Mexico City, Mexico
Added 2 new sites: Fountain Hill, Pennsylvania, Coswig, Germany
Added 4 new sites: Sacramento, California, Miami, Florida, Nice, France and 1 more
Reduced from 14 to 11 sites
Added 2 new sites: Edina, Minnesota, Seneca, South Carolina
Added 1 new site: Edina, Minnesota
Added 7 new sites: Brownstown, Michigan, Dearborn, Michigan, Jackson, Michigan and 4 more
Added 1 new site: Pardubice, Czechia
Added 20 new sites: La Jolla, California, Atlanta, Georgia, Kurralta Park, Australia and 17 more
Added 2 new sites: Kaohsiung City, Taiwan, Taiyuan, Taiwan
Added 3 new sites: Leeds, United Kingdom, Manchester, United Kingdom, Plymouth, United Kingdom
Eligibility criteria have been updated
Added 39 new sites: Duarte, California, Boston, Massachusetts, Boston, Massachusetts and 36 more
Added 3 new sites: Salt Lake City, Utah, Rzeszów, Poland, Bratislava, Slovakia
Added 2 new sites: Gastonia, North Carolina, Goiânia, Brazil
Added 3 new sites: Paramus, New Jersey, Lake Success, New York, The Bronx, New York
Reduced from 28 to 25 sites
Reduced from 28 to 25 sites
Reduced from 11 to 8 sites
Added 2 new sites: Orland Park, Illinois, Wilmington, North Carolina
Added 23 new sites: Indianapolis, Indiana, Columbus, Ohio, Dallas, Texas and 20 more
Reduced from 18 to 12 sites
Eligibility criteria have been updated
Added 1 new site: Boston, Massachusetts
Added 1 new site: Southaven, Mississippi
Added 1 new site: Lo Barnechea, Chile
Added 5 new sites: Little Rock, Arkansas, Stanford, California, Boston, Massachusetts and 2 more
Added 4 new sites: Memphis, Tennessee, Hefei, China, Bogota, Colombia and 1 more
Added 1 new site: Melbourne, Australia
Added 2 new sites: New York, New York, Houston, Texas
Added 1 new site: São Paulo, Brazil
Added 4 new sites: Boston, Massachusetts, Barcelona, Spain, Madrid, Spain and 1 more
Target enrollment decreased from 96 to 40
Eligibility criteria have been updated
Eligibility criteria have been updated
Added 9 new sites: Bahía Blanca, Argentina, Buenos Aires, Argentina, Buenos Aires, Argentina and 6 more
Eligibility criteria have been updated
Added 1 new site: Katowice, Poland
Added 4 new sites: Rochester, New York, Darlinghurst, Australia, Cuneo, Italy and 1 more
Added 44 new sites: Los Angeles, California, Orange, California, Sacramento, California and 41 more
Added 8 new sites: Salzburg, Austria, Curitiba, Brazil, Palermo, Italy and 5 more
Added 6 new sites: Houston, Texas, Heidelberg, Australia, Graz, Austria and 3 more
Added 1 new site: Winston-Salem, North Carolina
Added 8 new sites: Bodelwyddan, United Kingdom, Coventry, United Kingdom, Ipswich, United Kingdom and 5 more
Added 3 new sites: Rolling Meadows, Illinois, Iowa City, Iowa, Temple, Texas
Added 4 new sites: Sacramento, California, Miami, Florida, Nice, France and 1 more
Added 2 new sites: Tours, France, London, United Kingdom
Added 4 new sites: Nedlands, Australia, South Brisbane, Australia, Stockholm, Sweden and 1 more
Added 4 new sites: Sacramento, California, Miami, Florida, Nice, France and 1 more
Eligibility criteria have been updated
Added 3 new sites: Tampa, Florida, Snellville, Georgia, Chapel Hill, North Carolina
Target enrollment increased from 12 to 15
Added 1 new site: Maitland, Florida
Eligibility criteria have been updated
Added 2 new sites: Chapel Hill, North Carolina, Marburg, Germany
Added 20 new sites: Daphne, Alabama, Daphne, Alabama, Fairhope, Alabama and 17 more
Added 1 new site: Chicago, Illinois
Reduced from 77 to 74 sites
Added 2 new sites: Dallas, Texas, Lewisville, Texas
Reduced from 76 to 47 sites
Target enrollment decreased from 150 to 54
Eligibility criteria have been updated
Added 2 new sites: Bethesda, Maryland, Tainan, Taiwan
Added 2 new sites: Memphis, Tennessee, Houston, Texas
Added 7 new sites: Santa Ana, California, Miami, Florida, Lansing, Michigan and 4 more
Added 3 new sites: Rolling Meadows, Illinois, Iowa City, Iowa, Temple, Texas
Eligibility criteria have been updated
Added 8 new sites: Salzburg, Austria, Curitiba, Brazil, Palermo, Italy and 5 more
Eligibility criteria have been updated
Added 1 new site: Winston-Salem, North Carolina
Added 2 new sites: Tampa, Florida, Nashville, Tennessee
Added 1 new site: Edina, Minnesota
Added 3 new sites: Rolling Meadows, Illinois, Iowa City, Iowa, Temple, Texas
Added 3 new sites: Bergamo, Italy, Milan, Italy, Pisa, Italy
Moved from Phase 1 to Phase 1, Phase 2
Added 6 new sites: Phoenix, Arizona, Duarte, California, Aurora, Colorado and 3 more
Target enrollment increased from 60 to 275
Eligibility criteria have been updated
Added 2 new sites: Bemidji, Minnesota, Edina, Minnesota
Eligibility criteria have been updated
Added 2 new sites: Edina, Minnesota, Saint Paul, Minnesota
Eligibility criteria have been updated
Target enrollment decreased from 54 to 17
Eligibility criteria have been updated
Added 8 new sites: Kutaisi, Georgia, Tbilisi, Georgia, Tbilisi, Georgia and 5 more
Added 1 new site: Chicago, Illinois
Added 1 new site: Greenfield, Wisconsin
Reduced from 11 to 9 sites
Added 14 new sites: Beijing, China, Chongqing, China, Dijon, France and 11 more
Added 8 new sites: Los Angeles, California, Orange, California, Palo Alto, California and 5 more
Eligibility criteria have been updated
Eligibility criteria have been updated
Reduced from 236 to 232 sites
Added 13 new sites: Pleven, Bulgaria, Pleven, Bulgaria, Sofia, Bulgaria and 10 more
Added 1 new site: Birmingham, United Kingdom
Added 5 new sites: Pleven, Bulgaria, Tbilisi, Georgia, Palermo, Italy and 2 more
Added 5 new sites: Mostar, Bosnia and Herzegovina, Rustavi, Georgia, Krakow, Poland and 2 more
Added 17 new sites: Kogarah, Australia, Sofia, Bulgaria, Veliko Tarnovo, Bulgaria and 14 more
Added 2 new sites: Montreal, Canada, Ottawa, Canada
Eligibility criteria have been updated
Added 2 new sites: Mississauga, Canada, Oakville, Canada
Added 1 new site: Washington D.C., District of Columbia
Added 2 new sites: Reno, Nevada, Lubbock, Texas
Added 7 new sites: New York, New York, Katowice, Poland, Hwasun, South Korea and 4 more
Added 4 new sites: Ann Arbor, Michigan, Houston, Texas, Tacoma, Washington and 1 more
Added 6 new sites: New Haven, Connecticut, Hillsborough, North Carolina, Winston-Salem, North Carolina and 3 more
Added 5 new sites: O'Fallon, Illinois, O'Fallon, Illinois, Springfield, Illinois and 2 more
Added 8 new sites: Glendale, California, Batumi, Georgia, Kutaisi, Georgia and 5 more
Reduced from 171 to 162 sites
Added 3 new sites: New York, New York, Pessac, France, Taichung, Taiwan
Added 21 new sites: Los Angeles, California, Orange, California, Fort Worth, Texas and 18 more
Added 1 new site: Edina, Minnesota
Eligibility criteria have been updated
Added 3 new sites: Beijing, China, Beijing, China, Hanover, Germany
Eligibility criteria have been updated
Added 1 new site: Valencia, Spain
Added 1 new site: Gainesville, Florida
Added 1 new site: Sydney, Australia
Added 1 new site: Chandler, Arizona
Added 3 new sites: Boston, Massachusetts, Dresden, Germany, Barcelona, Spain
Added 1 new site: San Francisco, California
Added 19 new sites: Birmingham, Alabama, Stanford, California, Denver, Colorado and 16 more
Target enrollment increased from 25 to 56
Eligibility criteria have been updated
Added 6 new sites: Chermside, Australia, Rennes, France, Amiens, France and 3 more
Added 8 new sites: Hialeah, Florida, Kissimmee, Florida, Greensboro, North Carolina and 5 more
Added 1 new site: Porto Alegre, Brazil
Added 1 new site: Atlanta, Georgia
Added 2 new sites: Calgary, Canada, Petah Tikva, Israel
Eligibility criteria have been updated
Added 2 new sites: Omaha, Nebraska, Oakville, Canada
Expanded from 8 to 9 sites
Added 1 new site: Parkville, Australia
Added 1 new site: Warsaw, Poland
Added 1 new site: St Louis, Missouri
Added 2 new sites: Dallas, Texas, Oxford, United Kingdom
Added 1 new site: San Diego, California
Eligibility criteria have been updated
Added 3 new sites: Belgrade, Serbia, Taipei, Taiwan, Birmingham, United Kingdom
Reduced from 67 to 65 sites
Added 3 new sites: Belgrade, Serbia, Taipei, Taiwan, Birmingham, United Kingdom
Reduced from 28 to 26 sites
Added 4 new sites: Rosario, Argentina, Vienna, Austria, Campinas, Brazil and 1 more
Added 18 new sites: Phoenix, Arizona, Loma Linda, California, Palo Alto, California and 15 more
Eligibility criteria have been updated
Added 1 new site: San Juan, Puerto Rico
Added 1 new site: Humble, Texas
Added 1 new site: Ottawa, Canada
Added 3 new sites: Oxnard, California, Walnut Creek, California, Stuart, Florida
Eligibility criteria have been updated
Target enrollment decreased from 110 to 58
Eligibility criteria have been updated
Added 1 new site: Birmingham, Alabama
Eligibility criteria have been updated
Added 3 new sites: Salzburg, Austria, Palermo, Italy, Bursa, Turkey (Türkiye)
Eligibility criteria have been updated
Added 5 new sites: Toronto, Canada, Pécs, Hungary, Szeged, Hungary and 2 more
Added 1 new site: Seoul, South Korea
Added 9 new sites: Austin, Texas, Vienna, Austria, Curitiba, Brazil and 6 more
Added 3 new sites: Rolling Meadows, Illinois, Iowa City, Iowa, Temple, Texas
Added 3 new sites: Modena, Italy, Gdansk, Poland, Lodz, Poland
Added 7 new sites: Birmingham, Alabama, Los Angeles, California, Washington D.C., District of Columbia and 4 more
Added 1 new site: Irbid, Jordan
Target enrollment increased from 47 to 113
Eligibility criteria have been updated
Added 1 new site: New York, New York
Added 3 new sites: Brussels, Belgium, Leuven, Belgium, Athens, Greece
Eligibility criteria have been updated
Added 11 new sites: Scottsdale, Arizona, Los Angeles, California, Orange, California and 8 more
Added 2 new sites: Montreal, Canada, Ottawa, Canada
Eligibility criteria have been updated
Added 2 new sites: Cologne, Germany, Düsseldorf, Germany
Eligibility criteria have been updated
Target enrollment decreased from 66 to 17
Added 3 new sites: Bamberg, Germany, Berlin, Germany, Freiburg im Breisgau, Germany
Added 1 new site: Ottawa, Canada
Added 1 new site: Nangang, China
Added 3 new sites: Phoenix, Arizona, Buenos Aires, Argentina, Ottawa, Canada
Added 2 new sites: Nashville, Tennessee, Taipei, Taiwan
Eligibility criteria have been updated
Target enrollment increased from 12 to 36
Added 1 new site: Hanover, Germany
Target enrollment increased from 24 to 48
Added 1 new site: Brasília, Brazil
Eligibility criteria have been updated
Added 1 new site: Kingston, Canada
Added 1 new site: Valencia, Spain
Reduced from 19 to 17 sites
Target enrollment decreased from 28 to 19
Added 17 new sites: Glendale, Arizona, Beverly Hills, California, Canoga Park, California and 14 more
Eligibility criteria have been updated
Added 4 new sites: Athens, Greece, Chamberí, Spain, Madrid, Spain and 1 more
Added 2 new sites: São Paulo, Brazil, Ahmedabad, India
Added 6 new sites: Miami, Florida, Durham, North Carolina, Oklahoma City, Oklahoma and 3 more
Added 4 new sites: New York, New York, Ribeirão Preto, Brazil, São Paulo, Brazil and 1 more
Target enrollment decreased from 470 to 390
Eligibility criteria have been updated
Added 4 new sites: Washington D.C., District of Columbia, Yenişehir, Turkey (Türkiye), Liverpool, United Kingdom and 1 more
Added 1 new site: Davis, California
Target enrollment decreased from 750 to 377
Reduced from 10 to 8 sites
Added 19 new sites: Clovis, California, Los Angeles, California, Washington D.C., District of Columbia and 16 more
Reduced from 40 to 38 sites
Eligibility criteria have been updated
Added 34 new sites: Birmingham, Alabama, Phoenix, Arizona, Tucson, Arizona and 31 more
Eligibility criteria have been updated
Added 15 new sites: Orange, California, Columbus, Ohio, Philadelphia, Pennsylvania and 12 more
Added 1 new site: Charlottesville, Virginia
Eligibility criteria have been updated
Added 1 new site: Tbilisi, Georgia
Eligibility criteria have been updated
Added 13 new sites: New Hyde Park, New York, New York, New York, New York, New York and 10 more
Added 1 new site: Krakow, Poland
Added 22 new sites: Boca Raton, Florida, Lexington, Kentucky, New Orleans, Louisiana and 19 more
Added 7 new sites: Sun City, Arizona, Chicago, Illinois, Indianapolis, Indiana and 4 more
Added 4 new sites: Roseville, California, Milwaukee, Wisconsin, San Miguel de Tucumán, Argentina and 1 more
Added 25 new sites: Phoenix, Arizona, Los Angeles, California, Sacramento, California and 22 more
Target enrollment decreased from 150 to 111
Eligibility criteria have been updated
Added 22 new sites: Denver, Colorado, Austin, Texas, Buenos Aires, Argentina and 19 more
Eligibility criteria have been updated
Added 1 new site: Orlando, Florida
Added 2 new sites: Chicago, Illinois, Charlottesville, Virginia
Added 1 new site: Hamburg, Germany
Added 155 new sites: Birmingham, Alabama, Phoenix, Arizona, Los Angeles, California and 152 more
Eligibility criteria have been updated
Added 3 new sites: Bismarck, North Dakota, Fargo, North Dakota, Fargo, North Dakota
Added 1 new site: Münster, Germany
Added 3 new sites: Orlando, Florida, Warsaw, Poland, Ivano-Frankivsk, Ukraine
Eligibility criteria have been updated
Added 1 new site: Orlando, Florida
Target enrollment increased from 122 to 200
Added 1 new site: Barcelona, Spain
Added 1 new site: Westmead, Australia
Added 1 new site: Winston-Salem, North Carolina
Added 21 new sites: Denver, Colorado, Austin, Texas, Buenos Aires, Argentina and 18 more
Eligibility criteria have been updated
Eligibility criteria have been updated
Eligibility criteria have been updated
Target enrollment increased from 160 to 210
Eligibility criteria have been updated
Target enrollment increased from 60 to 100
Target enrollment decreased from 24 to 12
Eligibility criteria have been updated
Eligibility criteria have been updated
Added 4 new sites: Carlsbad, California, Las Vegas, Nevada, Thessaloniki, Greece and 1 more
Added 2 new sites: Montreal, Canada, Ottawa, Canada
Eligibility criteria have been updated
Added 1 new site: Liège, Belgium
Added 25 new sites: Clearwater, Florida, New Brunswick, New Jersey, New York, New York and 22 more
Added 1 new site: Veliko Tarnovo, Bulgaria
Added 29 new sites: Tucson, Arizona, Lancaster, California, Aurora, Colorado and 26 more
Added 38 new sites: Phoenix, Arizona, Newport Beach, California, Frederick, Maryland and 35 more
Target enrollment increased from 18 to 24
Eligibility criteria have been updated
Added 3 new sites: Cedar Rapids, Iowa, Cedar Rapids, Iowa, Great Falls, Montana
Eligibility criteria have been updated
Added 2 new sites: CABA, Argentina, Buenos Aires, Argentina
Eligibility criteria have been updated
Added 1 new site: Idaho Falls, Idaho
Added 2 new sites: Kogarah, Australia, Kaohsiung City, Taiwan
Reduced from 8 to 5 sites
Added 1 new site: Zurich, Switzerland
Target enrollment increased from 115 to 160
Added 1 new site: Zurich, Switzerland
Target enrollment increased from 115 to 160
Added 1 new site: Rochester, New York
Added 4 new sites: La Tronche, France, Vandœuvre-lès-Nancy, France, Sapporo, Japan and 1 more
Added 2 new sites: Torrance, California, Pittsburgh, Pennsylvania
Added 6 new sites: Bron, France, Nantes, France, Toulouse, France and 3 more
Added 1 new site: Hamburg, Germany
Added 3 new sites: Reno, Nevada, The Bronx, New York, Murray, Utah
Added 2 new sites: São Paulo, Brazil, Kaohsiung City, Taiwan
Reduced from 71 to 59 sites
Added 25 new sites: New Lambton Heights, Australia, Sydney, Australia, Launceston, Australia and 22 more
Eligibility criteria have been updated
Added 12 new sites: Winston-Salem, North Carolina, Melbourne, Australia, Haskovo, Bulgaria and 9 more
Added 1 new site: Doral, Florida
Added 4 new sites: Bobigny, France, Athens, Greece, Santiago de Compostela, Spain and 1 more
Added 16 new sites: Dothan, Alabama, St. Petersburg, Florida, Rock Hill, South Carolina and 13 more
Added 7 new sites: Englewood, Colorado, Lawrenceville, Georgia, Jackson, Mississippi and 4 more
Added 6 new sites: Ancenis, France, Angers, France, Châteaubriant, France and 3 more
Eligibility criteria have been updated
Added 7 new sites: Boston, Massachusetts, Charlestown, Massachusetts, Columbus, Ohio and 4 more
Eligibility criteria have been updated
Eligibility criteria have been updated
Added 6 new sites: Indianapolis, Indiana, Columbus, Ohio, Seattle, Washington and 3 more
Eligibility criteria have been updated
Eligibility criteria have been updated
Added 3 new sites: La Jolla, California, La Jolla, California, San Diego, California
Added 3 new sites: New Haven, Connecticut, Newark, New Jersey, New York, New York
Added 13 new sites: Aalst, Belgium, Ghent, Belgium, Plovdiv, Bulgaria and 10 more
Added 6 new sites: Pasadena, California, San Jose, California, Wichita, Kansas and 3 more
Added 2 new sites: Orchard Park, New York, Philadelphia, Pennsylvania
Added 1 new site: Houston, Texas
Added 4 new sites: Caba, Argentina, Serra, Brazil, Blumenau, Brazil and 1 more
Added 1 new site: London, United Kingdom
Added 1 new site: Wake Forest, North Carolina
Added 6 new sites: Manchester, Connecticut, Carmel, Indiana, Nashua, New Hampshire and 3 more
Added 6 new sites: Granada Hills, California, Victorville, California, Grand Prairie, Texas and 3 more
Added 2 new sites: Honolulu, Hawaii, Omaha, Nebraska
Reduced from 58 to 50 sites
Added 18 new sites: Denver, Colorado, Buenos Aires, Argentina, CABA, Argentina and 15 more
Added 1 new site: Philadelphia, Pennsylvania
Target enrollment increased from 40 to 55
Added 1 new site: Westmead, Australia
Added 1 new site: St Louis, Missouri
Eligibility criteria have been updated
Added 3 new sites: Brasília, Brazil, Belo Horizonte, Brazil, Dammam, Saudi Arabia
Added 2 new sites: Riyadh, Saudi Arabia, Riyadh, Saudi Arabia
Added 4 new sites: Vero Beach, Florida, Salvador, Brazil, Medellín, Colombia and 1 more
Added 1 new site: Barcelona, Spain
Eligibility criteria have been updated
Added 5 new sites: Chapel Hill, North Carolina, Columbus, Ohio, Houston, Texas and 2 more
Added 3 new sites: Columbus, Ohio, Nicosia, Cyprus, London, United Kingdom
Eligibility criteria have been updated
Added 1 new site: Seattle, Washington
Added 3 new sites: Göttingen, Germany, Roma, Italy, London, United Kingdom
Added 4 new sites: Vienna, Austria, Ramat Gan, Israel, Messina, Italy and 1 more
Added 5 new sites: Fayetteville, North Carolina, Houston, Texas, Krakow, Poland and 2 more
Added 3 new sites: Homburg, Germany, Würzburg, Germany, Leeds, United Kingdom
Reduced from 8 to 5 sites
Added 3 new sites: Riverside, California, New York, New York, Houston, Texas
Added 1 new site: Westmead, Australia
Target enrollment increased from 16 to 26
Eligibility criteria have been updated
Added 3 new sites: La Jolla, California, Honolulu, Hawaii, Würzburg, Germany
Added 17 new sites: Multiple Locations, Austria, Multiple Locations, Belgium, Multiple Locations, Croatia and 14 more
Added 4 new sites: Belgrano, Argentina, Salvador, Brazil, Guadalajara, Mexico and 1 more
Added 1 new site: Miami, Florida
Added 2 new sites: Lübeck, Germany, London, United Kingdom
Target enrollment increased from 30 to 60
Eligibility criteria have been updated
Target enrollment increased from 6 to 13
Reduced from 128 to 106 sites
Added 7 new sites: Voorhees Township, New Jersey, Wilmington, North Carolina, Sydney, Canada and 4 more
Added 2 new sites: Clearwater, Florida, Trois-Rivières, Canada
Added 17 new sites: Multiple Locations, Austria, Multiple Locations, Belgium, Multiple Locations, Croatia and 14 more
Added 2 new sites: Henan, China, Seoul, South Korea
Eligibility criteria have been updated
Added 15 new sites: La Jolla, California, Garran, Australia, Leuven, Belgium and 12 more
Added 5 new sites: Berlin, Germany, Freiburg im Breisgau, Germany, Leipzig, Germany and 2 more
Added 1 new site: Philadelphia, Pennsylvania
Added 1 new site: Boston, Massachusetts
Added 5 new sites: Randwick, Australia, Parkville, Australia, Calgary, Canada and 2 more
Added 7 new sites: Osaka, Japan, Tokyo, Japan, Tokyo, Japan and 4 more
Added 14 new sites: Chicago, Illinois, New York, New York, Austin, Texas and 11 more
Added 1 new site: Chicago, Illinois
Eligibility criteria have been updated
Added 1 new site: Dallas, Texas
Target enrollment increased from 256 to 786
Eligibility criteria have been updated
Added 2 new sites: Ghent, Belgium, Kaohsiung City, Taiwan
Added 3 new sites: Spokane, Washington, Diest, Belgium, Kumamoto, Japan
Added 2 new sites: Gainesville, Florida, Baltimore, Maryland
Added 14 new sites: Chicago, Illinois, New York, New York, Austin, Texas and 11 more
Eligibility criteria have been updated
Added 5 new sites: Ruskin, Florida, Tampa, Florida, Tampa, Florida and 2 more
Added 2 new sites: Minneapolis, Minnesota, Sturgeon Bay, Wisconsin
Added 6 new sites: Monroe, Louisiana, Houston, Texas, Red Oak, Texas and 3 more
Eligibility criteria have been updated
Added 1 new site: Yamagata, Japan
Added 2 new sites: Maidstone, United Kingdom, Oxford, United Kingdom
Eligibility criteria have been updated
Added 6 new sites: Seattle, Washington, CABA, Argentina, São Paulo, Brazil and 3 more
Added 1 new site: Málaga, Spain
Eligibility criteria have been updated
Added 3 new sites: Worcester, Massachusetts, Albuquerque, New Mexico, New York, New York
Added 30 new sites: Mostar, Bosnia and Herzegovina, Haryāna, India, Raipur, India and 27 more
Added 2 new sites: Chieti, Italy, Lviv, Ukraine
Reduced from 89 to 82 sites
Added 6 new sites: São Paulo, Brazil, Frankfurt am Main, Germany, Bonn, Germany and 3 more
Eligibility criteria have been updated
Added 5 new sites: Los Angeles, California, Los Angeles, California, New York, New York and 2 more
Target enrollment increased from 884 to 952
Eligibility criteria have been updated
Reduced from 43 to 38 sites
Added 4 new sites: Scottsdale, Arizona, Tucson, Arizona, La Jolla, California and 1 more
Added 15 new sites: La Jolla, California, Garran, Australia, Leuven, Belgium and 12 more
Added 5 new sites: Berlin, Germany, Freiburg im Breisgau, Germany, Leipzig, Germany and 2 more
Added 10 new sites: Changsha, China, Shanghai, China, Debrecen, Hungary and 7 more
Added 1 new site: Metz, France
Reduced from 178 to 171 sites
Added 8 new sites: Newark, Delaware, Houston, Texas, Roeselare, Belgium and 5 more
Target enrollment increased from 448 to 540
Added 3 new sites: Alexandroupoli, Greece, Heraklion, Greece, Taipei, Taiwan
Reduced from 193 to 190 sites
Added 2 new sites: Phoenix, Arizona, Macomb, Michigan
Added 3 new sites: Augusta, Georgia, Indianapolis, Indiana, Salt Lake City, Utah
Added 2 new sites: Westmead, Australia, Lille, France
Eligibility criteria have been updated
Added 1 new site: Phoenix, Arizona
Added 17 new sites: Miami, Florida, Ann Arbor, Michigan, Minneapolis, Minnesota and 14 more
Added 1 new site: Tampa, Florida
Added 6 new sites: San Francisco, California, Iowa City, Iowa, Columbus, Ohio and 3 more
Added 4 new sites: Winnipeg, Canada, Kingston, Canada, Montreal, Canada and 1 more
Added 6 new sites: Chicago, Illinois, New York, New York, Montreal, Canada and 3 more
Added 1 new site: Washington D.C., District of Columbia
Added 3 new sites: Lutherville, Maryland, Hamilton, New Jersey, Richmond, Virginia
Added 5 new sites: Yerevan, Armenia, Lausanne, Switzerland, Lucerne, Switzerland and 2 more
Added 2 new sites: Gloucester, United Kingdom, Sunderland, United Kingdom
Added 1 new site: Springfield, Illinois
Added 1 new site: New York, New York
Added 3 new sites: Itami, Japan, Hamamatsu, Japan, Kagoshima, Japan
Added 1 new site: Tacoma, Washington
Added 5 new sites: Birmingham, Alabama, Baton Rouge, Louisiana, Dallas, Texas and 2 more
Added 9 new sites: Austin, Texas, Graz, Austria, Lens, France and 6 more
Reduced from 163 to 161 sites
Moved from N/A to Phase 2
Eligibility criteria have been updated
Added 5 new sites: Denver, Colorado, Detroit, Michigan, Nashville, Tennessee and 2 more
Added 5 new sites: Atlanta, Georgia, Boston, Massachusetts, Toronto, Canada and 2 more
Added 2 new sites: Pittsburgh, Pennsylvania, Salamanca, Spain
Target enrollment decreased from 700 to 539
Eligibility criteria have been updated
Eligibility criteria have been updated
Added 1 new site: Atlanta, Georgia
Eligibility criteria have been updated
Eligibility criteria have been updated
Added 1 new site: Columbus, Ohio
Moved from Phase 3 to N/A
Target enrollment increased from 272 to 426
Eligibility criteria have been updated
Added 2 new sites: Hollywood, Florida, Orangeburg, South Carolina
Added 5 new sites: Toulouse, France, Hiroshima, Japan, Utrecht, Netherlands and 2 more
Eligibility criteria have been updated
Eligibility criteria have been updated
Added 1 new site: Birmingham, United Kingdom
Target enrollment increased from 106 to 192
Eligibility criteria have been updated
Added 4 new sites: Tübingen, Germany, Leiden, Netherlands, Auckland, New Zealand and 1 more
Added 1 new site: New Haven, Connecticut
Eligibility criteria have been updated
Added 7 new sites: Washington D.C., District of Columbia, Cincinnati, Ohio, Salt Lake City, Utah and 4 more
Added 1 new site: San Francisco, California
Target enrollment increased from 10 to 19
Added 1 new site: Atlanta, Georgia
Added 1 new site: Atlanta, Georgia
Added 2 new sites: Seoul, South Korea, Seoul, South Korea
Eligibility criteria have been updated
Added 2 new sites: Los Angeles, California, Oslo, Norway
Added 2 new sites: Palo Alto, California, Beijing, China
Added 7 new sites: Boston, Massachusetts, Potsdam, New York, Sherbrooke, Canada and 4 more
Added 1 new site: Saint-Denis, France
Added 1 new site: Eldoret, Kenya
Added 2 new sites: Pittsburgh, Pennsylvania, Skawina, Poland
Target enrollment decreased from 94 to 32
Eligibility criteria have been updated
Added 9 new sites: Philadelphia, Pennsylvania, Seattle, Washington, Bron, France and 6 more
Added 1 new site: Seoul, South Korea
Added 218 new sites: Phoenix, Arizona, La Jolla, California, Los Angeles, California and 215 more
Reduced from 74 to 72 sites
Added 12 new sites: San Antonio, Texas, Barranquilla, Colombia, Cali, Colombia and 9 more
Added 9 new sites: Los Angeles, California, Adelaide, Australia, Clayton, Australia and 6 more
Added 15 new sites: Stuart, Florida, Bethesda, Maryland, Tyler, Texas and 12 more
Eligibility criteria have been updated
Added 1 new site: Dundee, United Kingdom
Eligibility criteria have been updated
Added 1 new site: Gdansk, Poland
Added 1 new site: Columbus, Ohio
Added 1 new site: São Paulo, Brazil
Eligibility criteria have been updated
Added 7 new sites: Washington D.C., District of Columbia, Cincinnati, Ohio, Salt Lake City, Utah and 4 more
Added 2 new sites: Mexico City, Mexico, Gdansk, Poland
Eligibility criteria have been updated
Added 2 new sites: Los Angeles, California, Indianapolis, Indiana
Added 3 new sites: St. Petersburg, Florida, Rincon, Georgia, Houston, Texas
Added 1 new site: Houston, Texas
Added 2 new sites: Milan, Italy, Leiden, Netherlands
Target enrollment decreased from 10 to 7
Added 9 new sites: Los Angeles, California, Adelaide, Australia, Clayton, Australia and 6 more
Added 15 new sites: Stuart, Florida, Bethesda, Maryland, Tyler, Texas and 12 more
Eligibility criteria have been updated
Added 1 new site: Baltimore, Maryland
Added 1 new site: Compiègne, France
Added 1 new site: Saint Paul, Minnesota
Eligibility criteria have been updated
Eligibility criteria have been updated
Reduced from 130 to 120 sites
Added 5 new sites: Chicago, Illinois, Durham, North Carolina, Padova, Italy and 2 more
Added 15 new sites: Tbilisi, Georgia, Shimla, India, Mexico City, Mexico and 12 more
Added 4 new sites: Lewisville, Texas, Zlín, Czechia, Siegen, Germany and 1 more
Eligibility criteria have been updated
Added 3 new sites: Tbilisi, Georgia, Esztergom, Hungary, Niš, Serbia
Added 2 new sites: Scottsdale, Arizona, Maitland, Florida
Added 1 new site: Tsu, Japan
Target enrollment increased from 100 to 120
Eligibility criteria have been updated
Added 1 new site: Dundee, United Kingdom
Eligibility criteria have been updated
Added 2 new sites: Duarte, California, Zion, Illinois
Added 2 new sites: Ningbo, China, Suita-Shi, Japan
Added 1 new site: Bordeaux, France
Added 3 new sites: Hyderabad, India, Hyderabad, India, Surat, India
Added 1 new site: Kansas City, Missouri
Added 8 new sites: Beijing, China, Beijing, China, Chengdu, China and 5 more
Eligibility criteria have been updated
Added 2 new sites: Chaïdári, Greece, Ioannina, Greece
Added 14 new sites: Newport Beach, California, New Haven, Connecticut, New York, New York and 11 more
Added 3 new sites: New York, New York, Afula, Israel, Ramat Gan, Israel
Added 111 new sites: Lewes, Delaware, Millville, Delaware, Newark, Delaware and 108 more
Eligibility criteria have been updated
Eligibility criteria have been updated
Added 16 new sites: Indianapolis, Indiana, Melbourne, Australia, Bron, France and 13 more
Added 16 new sites: Indianapolis, Indiana, Melbourne, Australia, Bron, France and 13 more
Added 2 new sites: New Haven, Connecticut, East Brunswick, New Jersey
Added 2 new sites: Hollywood, Florida, Orangeburg, South Carolina
Added 6 new sites: Liverpool, Australia, Parkville, Australia, Taichung, Taiwan and 3 more
Target enrollment increased from 376 to 428
Added 3 new sites: Milwaukee, Wisconsin, Stuttgart, Germany, Braunschweig, Germany
Added 11 new sites: Exochi, Greece, Lima, Peru, Surco, Peru and 8 more
Added 1 new site: Greeley, Colorado
Eligibility criteria have been updated
Added 2 new sites: Salerno, Italy, Salamanca, Spain
Target enrollment decreased from 100 to 79
Added 10 new sites: Buenos Aires, Argentina, Buenos Aires, Argentina, Córdoba, Argentina and 7 more
Added 2 new sites: South Gate, California, Winnipeg, Canada
Added 5 new sites: Garden Grove, California, Augusta, Georgia, Valhalla, New York and 2 more
Eligibility criteria have been updated
Added 62 new sites: Phoenix, Arizona, Phoenix, Arizona, Tucson, Arizona and 59 more
Added 2 new sites: Livingston, New Jersey, Busan, South Korea
Added 9 new sites: Los Angeles, California, Adelaide, Australia, Clayton, Australia and 6 more
Added 7 new sites: Bethesda, Maryland, Nîmes, France, Mannheim, Germany and 4 more
Added 1 new site: Santander, Spain
Added 26 new sites: Perth, Australia, St Leonards, Australia, Sydney, Australia and 23 more
Reduced from 16 to 14 sites
Eligibility criteria have been updated
Added 2 new sites: Barcelona, Spain, Málaga, Spain
Added 7 new sites: Exton, Pennsylvania, Westmead, Australia, AT Albans, Australia and 4 more
Reduced from 124 to 104 sites
Added 2 new sites: The Bronx, New York, Seoul, South Korea
Target enrollment increased from 50 to 80
Moved from N/A to Early Phase 1
Added 2 new sites: Scottsdale, Arizona, Jacksonville, Florida
Eligibility criteria have been updated
Added 3 new sites: Birmingham, Alabama, Los Angeles, California, Cincinnati, Ohio
Target enrollment increased from 12 to 20
Eligibility criteria have been updated
Added 15 new sites: Fort Myers, Florida, Stuart, Florida, Dallas, Texas and 12 more
Target enrollment decreased from 10 to 7
Added 7 new sites: Palo Alto, California, Aurora, Colorado, Gainesville, Florida and 4 more
Target enrollment decreased from 580 to 170