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Charcot-Marie-Tooth Disease Clinical Trials Near Me

As of November 13, 2026, 26 Charcot-Marie-Tooth Disease clinical trials are recruiting now and 4 are not yet recruiting. In the US, 7 of them have at least 1 open site, across 20 states and Washington, DC. Enter your ZIP code below to see which are closest to you.

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All 26 Charcot-Marie-Tooth Disease trials and their US sites

Enter your ZIP code above to sort them by how far their nearest open site is from you.

  1. The Myelin Disorders Biorepository Project
    Most sites in California, Pennsylvania and Minnesota
    RecruitingChildren's Hospital of Philadelphia
    24US sites
    14 states
  2. Genetics of Charcot Marie Tooth (CMT) - Modifiers of CMT1A, New Causes of CMT2
    Most sites in California, Pennsylvania and Colorado
    RecruitingUniversity of Iowa
    18US sites
    16 states
  3. Natural History Evaluation of Charcot Marie Tooth Disease (CMT) Types CMT1B, CMT2A, CMT4A, CMT4C, and Others
    Most sites in California, Pennsylvania and Colorado
    RecruitingMichael Shy
    18US sites
    16 states
  4. Study of Intrathecal ELP-02 for Charcot-Marie-Tooth Disease Type 4J (CMT4J)
    Most sites in California and Iowa
    RecruitingPhase 1/2Ages 3-20Elpida Therapeutics SPC
    2US sites
    2 states
  5. A Natural History Study Seeks to Understand the Clinical, Genomic, Pharmacological, Laboratory, and Dietary Determinates of Pyrimidine and Purine Metabolism Disorders
    Only in Maryland
    RecruitingAges 1 Month-100National Human Genome Research Institute (NHGRI)
    1US site
  6. CMT Gait, Mobility, Balance - AOFAS Grant
    Only in Iowa
    RecruitingAges 25-55Bopha Chrea
    1US site
  7. Natural History Study for Charcot Marie Tooth Disease
    Only in New York
    RecruitingHereditary Neuropathy Foundation
    1US site
  8. A First in Human Study to Assess the Safety, Tolerability, and Pharmacokinetics of EDK060 in Adults With CMT1A.
    RecruitingPhase 1Ages 18-60Novartis Pharmaceuticals
    No US site yet
  9. A Multi-omic Approach to the Identification of Novel Biomarkers in Early Charcot-Marie-Tooth 1A Disease (CMT1A)
    RecruitingAges 10-30University Medical Center Goettingen
    No US site yet
  10. A Registered Cohort Study on Charcot-Marie-Tooth Disease
    RecruitingNing Wang, MD., PhD.
    No US site yet
  11. Assessment of a Portable Digital Device for Quantified Analysis of Markerless Walking in Volunteers With Neuromuscular Diseases or Asymptomatic Volunteers
    RecruitingAges 18-65Institut de Myologie, France
    No US site yet
  12. Assessments in Patients With Muscular Pathology and in Control Subjects : The ActiLiège Next Study
    RecruitingAges 1-80Centre Hospitalier Universitaire de Liege
    No US site yet
  13. AUTONOMOUS DISORDERS IN CMT
    RecruitingAges 18-65University Medical Center Goettingen
    No US site yet
  14. Clinical Trial Evaluating the Impact of an Intensive Rehabilitation Program Combined With Tendon Vibratory Stimulation on Functional Balance in Individuals With Charcot-Marie-Tooth Disease Type 1A
    RecruitingAges 18-65UGECAM PACA et Corse
    No US site yet
  15. Effects of Resistance Exercises in Hereditary Sensory-Motor Neuropathy (Charcot-Marie-Tooth Disease)
    RecruitingAges 15-29Universidad de La Frontera
    No US site yet
  16. Evaluate the Safety and Efficacy of EN001 in Patients With Charcot-Marie-Tooth Disease Type 1A(CMT1A) (Phase 1b: Open-label, Dose-escalation, Single-center; Phase 2a: Randomized, Double-blind, Placebo-controlled, Multicenter)
    RecruitingPhase 1/2Ages 19+ENCell
    No US site yet
  17. Gait Analysis Parameter and Upper Limb Evaluation in Adult Patients With Neurological or Metabolic Pathology
    RecruitingAges 18+Centre Hospitalier Universitaire de Liege
    No US site yet
  18. Genotype/Phenotype Correlation of MORC2 Mutations
    RecruitingAges 4+Hospices Civils de Lyon
    No US site yet
  19. High-Tech Rehabilitation Pathway for Chronic Adult Neuromuscular Diseases - Fit4MedRob-Chronic MND Project
    RecruitingAges 18-80Istituti Clinici Scientifici Maugeri SpA
    No US site yet
  20. Longitudinal Biomarkers With Selected Outcome Measures In CMT
    RecruitingAges 18-65University Medical Center Goettingen
    No US site yet
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Who runs the Charcot-Marie-Tooth Disease trials in the US, and what stage they are in

None of the 7 Charcot-Marie-Tooth Disease trials with a US site is in Phase 3, the last stage before a company can ask the FDA for approval. One more is an earlier Phase 1 or 2 test of safety and dosing. The remaining 6 have no drug phase, such as studies that follow people over time or test a device or a way of giving care. Companies run 1 of them, and universities, hospitals, foundations and government groups run 6. The most recently listed one first appeared on ClinicalTrials.gov on March 3, 2026.

Charcot-Marie-Tooth Disease trials in the US, state by state

Of the 7 Charcot-Marie-Tooth Disease trials with a US site, 6 accept children under 18. Their open sites are in 20 states and Washington, DC, most often California, Maryland and Iowa. A trial counts once in each state where it has an open site, and some trials accept both children and adults.

StateTrialsChildrenAdultsCities with the most
California444Palo Alto (4), Los Angeles (3), Orange (1), plus 3 more
Iowa434Iowa City (3), North Liberty (1)
Maryland444Baltimore (3), Bethesda (1)
Massachusetts333Boston (3)
Minnesota333Minneapolis (2), Maple Grove (1), Rochester (1)
New York333Rochester (2), New York (1)
North Carolina333Chapel Hill (2), Winston-Salem (1)
Ohio333Columbus (3), Akron (1)
Pennsylvania333Philadelphia (3), Pittsburgh (1)
Texas333Houston (3)
Show the other 11 states
Washington333Seattle (3)
Colorado222Aurora (2)
Connecticut222Hartford (2)
Florida222Miami (2)
Michigan222Ann Arbor (2)
Tennessee222Memphis (2)
District of Columbia111Washington D.C. (1)
Georgia111Atlanta (1)
Illinois111Chicago (1)
Utah111Salt Lake City (1)
Virginia111Charlottesville (1)

US hospitals running the most Charcot-Marie-Tooth Disease trials

Centers that run trials for a rare condition often see more people with it than most clinics do, so this list can also help you find doctors who know Charcot-Marie-Tooth Disease.

  1. Nationwide Children's HospitalColumbus, Ohio3 trials
  2. Seattle Children's HospitalSeattle, Washington3 trials
  3. Stanford UniversityPalo Alto, California3 trials
  4. University of IowaIowa City, Iowa3 trials
  5. University of PennsylvaniaPhiladelphia, Pennsylvania3 trials
  6. Cedars-Sinai Medical CenterLos Angeles, California2 trials
  7. Children's Hospital of PhiladelphiaPhiladelphia, Pennsylvania2 trials
  8. Harvard/Massachusetts General HospitalBoston, Massachusetts2 trials
  9. Houston Methodist HospitalHouston, Texas2 trials
  10. Johns Hopkins UniversityBaltimore, Maryland2 trials

Help getting to a Charcot-Marie-Tooth Disease trial far from home

Ask the study team whether the trial pays back travel, parking and hotel costs, because many sponsors do. The FDA's guidance on paying research volunteers says paying back these costs does not count as pressuring someone to join.

These nonprofits also help patients reach care, and each one sets its own rules.

Mercy Medical Angels
Pays for gas cards, ground rides and airline tickets anywhere in the US, and it lists clinical trials as a reason to travel. Household income at or below 300% of the federal poverty guidelines, and usually a trip of 50 miles or more each way.
Air Charity Network
Volunteer pilots in all 50 states fly patients for free in small private planes, and members also fly people taking part in clinical trials. You must be able to walk and sit upright for the flight, show financial need and have a backup plan if weather cancels it.
Ronald McDonald House
Gives families a room near the hospital while a child gets care, through 394 House programs around the world. Families of a sick child, with rules set by each local chapter.
Healthcare Hospitality Network
Keeps a map of hospitality houses near hospitals, and most member houses charge little or nothing to patients and families. Each house sets its own rules, so check with the house near your study site.

Program details were checked on each program's website on October 24, 2026.

Questions about finding a Charcot-Marie-Tooth Disease trial near you

Are there Charcot-Marie-Tooth Disease clinical trials near me?

As of November 13, 2026, 26 Charcot-Marie-Tooth Disease clinical trials are recruiting now and 4 are not yet recruiting. In the US, 7 of them have at least 1 open site, across 20 states and Washington, DC. Enter your ZIP code on this page to rank every one of them by the distance to its closest open site, with the sites shown on a map.

Which states have Charcot-Marie-Tooth Disease clinical trial sites?

Recruiting Charcot-Marie-Tooth Disease trials list open sites in 20 states and Washington, DC. California, Iowa and Maryland have the most, and the table on this page lists every state.

Are there Charcot-Marie-Tooth Disease trials for children near me?

Of the 7 Charcot-Marie-Tooth Disease trials with a US site, 6 accept children under 18. Their open sites are in 20 states and Washington, DC, most often California, Maryland and Iowa. Each trial sets its own age limits, so check the ages listed on a trial before you contact it.

Who pays for travel to a Charcot-Marie-Tooth Disease clinical trial?

Many trial sponsors pay back travel, parking and hotel costs, so ask the study team before you rule out a far-away site. The FDA's guidance says paying back these costs does not count as pressuring someone to join. Charities such as Mercy Medical Angels and Air Charity Network can also help with rides and flights.

What if there is no Charcot-Marie-Tooth Disease trial near me?

Some trials send staff to your home or use a local lab, so fewer visits happen at the study site. You can also sign up on this page to get an email when a Charcot-Marie-Tooth Disease trial opens a new site or changes status.

How is the distance to a trial site measured?

Distances are straight-line miles from the center of your ZIP code to each study site's listed location, not driving distance. Your browser looks up the ZIP code's coordinates with a free map service, Zippopotam.us, and the ZIP code is never sent to or stored by Trial Friend.

Source: ClinicalTrials.gov, trials with status Recruiting or Not yet recruiting. Refreshed every 6 hours; counts as of November 13, 2026. Sites that ClinicalTrials.gov lists as closed or withdrawn are left out. Children means the trial's age group includes people under 18.