Zero ad trackers.We never sell your data.

Duchenne Muscular Dystrophy Clinical Trials Near Me

As of October 12, 2026, 74 Duchenne Muscular Dystrophy clinical trials are recruiting or about to open (58 recruiting now, 16 opening soon). 29 of them have at least 1 open site in the United States, across 27 states. Enter your ZIP code to see which are closest to you.

Also on Trial Friend:Duchenne Muscular Dystrophy pageMatch Me

Trial Friend never receives or stores your ZIP code. Your browser looks up its location with a free map service.
Distance
Status
Ages
Phase
+45 more

All 58 Duchenne Muscular Dystrophy trials and their US sites

Enter your ZIP code above to sort them by how far their nearest open site is from you.

  1. Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT
    Phoenix Children's Hospital, Phoenix, Arizona; Arkansas Childrens Hospital, Little Rock, Arkansas; Loma Linda University Pediatric Subspecialty Clinics, Loma Linda, California and 28 more sites
    RecruitingAges 2+Run by Catalyst Pharmaceuticals, Inc.
  2. A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
    Arkansas Children's Hospital, Little Rock, Arkansas; University of California, Los Angeles Medical Center, Los Angeles, California; University of California, Davis, Sacramento, California and 9 more sites
    RecruitingPhase 1/2Ages 0 to 17Run by Solid Biosciences Inc.
  3. A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort
    Arkansas Children's Hospital, Little Rock, Arkansas; University of California, San Diego, La Jolla, California; University of California, Los Angeles, Los Angeles, California and 8 more sites
    RecruitingPhase 1Ages 2+Run by Sarepta Therapeutics, Inc.
  4. Duchenne Electronic Health Record Study
    Arkansas Children's Hospital, Little Rock, Arkansas; UC Davis Health, Sacramento, California; Children's Hospital Colorado, Aurora, Colorado and 7 more sites
    RecruitingRun by The Duchenne Registry
  5. Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials
    UC Davis, Sacramento, California; Children's National, Washington D.C., District of Columbia; Lurie Children's, Chicago, Illinois and 6 more sites
    RecruitingRun by Vanderbilt University Medical Center
  6. Biomarker Development for Muscular Dystrophies
    Brigham and Women's Hospital, Boston, Massachusetts; Massachusetts General Hospital, Boston, Massachusetts; Wake Forest University, Winston-Salem, North Carolina and 1 more site
    RecruitingAges 5+Run by Massachusetts General Hospital
  7. Once Weekly Infant Corticosteroid Trial for DMD
    Lurie Children's Hospital of Chicago, Chicago, Illinois; University of Cincinnati, Cincinnati, Ohio; Nationwide Children's Hospital, Columbus, Ohio and 1 more site
    RecruitingPhase 4Ages 1 Month to 30 MonthsRun by Anne M. Connolly
  8. The Baby Duchenne Study: Characterizing Developmental and Clinical Outcomes in the First Three Years in Children With Duchenne Muscular Dystrophy
    University of Rochester, Rochester, New York; Stony Brook Medicine, Stony Brook, New York; Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio and 1 more site
    RecruitingAges 0 Days to 3Run by University of Rochester
  9. A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)
    Arkansas Children's Hospital, Little Rock, Arkansas; Neurology Rare Disease Center, Flower Mound, Texas; Children's Hospital of the King's Daughters, Norfolk, Virginia
    RecruitingPhase 3Ages 7 to 11Run by Solid Biosciences Inc.
  10. Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
    Stanford University, Palo Alto, California; Boston Children's Hospital, Boston, Massachusetts; Columbia University Irving Medical Center, New York, New York
    RecruitingAges 5+Run by Columbia University
  11. Modulation of SERCA2a of Intra-Myocytic Calcium Trafficking in Cardiomyopathy Secondary to Duchenne Muscular Dystrophy
    The University of Kansas Medical Center, Kansas City, Kansas; Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio; Nationwide Children's Hospital, Columbus, Ohio
    RecruitingPhase 1Ages 18+Run by Sardocor Corp.
  12. Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study
    MD Rare Disease Research, LLC, Atlanta, Georgia; University of Iowa Children's Hospital, Iowa City, Iowa
    RecruitingPhase 2/3Ages 7+Run by Italfarmaco
  13. Magnetic Resonance Imaging and Biomarkers for Muscular Dystrophy
    University of Florida, Gainesville, Florida; Oregon Health and Science University, Portland, Oregon
    RecruitingAges 5 to 62Run by University of Florida
  14. Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53)
    Arkansas Children's Hospital, Little Rock, Arkansas; Rare Disease Research LLC, Atlanta, Georgia
    RecruitingPhase 1/2Ages 4 to 18Run by Wave Life Sciences USA, Inc.
  15. PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)
    Arkansas Children's Hospital, Little Rock, Arkansas; Washington University School of Medicine, St Louis, Missouri
    RecruitingPhase 1/2Ages 2 to 7Run by Precision BioSciences, Inc.
  16. DMD Voice: Qualitative Interviews With Patients and Caregivers
    Red Nucleus, Yardley, Pennsylvania
    RecruitingAges 10+Run by Red Nucleus Enterprise Solutions, LLC
  17. Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
    Rare Disease Research, LLC, Hillsborough, North Carolina
    RecruitingPhase 3Ages 4 to 18Run by Dyne Therapeutics
  18. Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy Patients
    University of Florida, Gainesville, Florida
    RecruitingPhase 2Ages 6+Run by University of Florida
  19. Extracellular RNA Biomarkers of Duchenne Muscular Dystrophy
    Massachusetts General Hospital, Boston, Massachusetts
    RecruitingAges 5+Run by Massachusetts General Hospital
  20. Molecular Analysis of Patients With Neuromuscular Disease
    Boston Children's Hospital, Boston, Massachusetts
    RecruitingAges 1 Week to 100Run by Boston Children's Hospital
Get an email when Duchenne Muscular Dystrophy trials change

New trials, status changes and new sites, straight from ClinicalTrials.gov. Unsubscribe anytime.

You'll get new recruiting trials, changes to trials, FDA decisions and condition news for Duchenne Muscular Dystrophy. Turn any of these off from the link in every email.

We never share your email. Unsubscribe anytime. Privacy policy

Where Duchenne Muscular Dystrophy trials are recruiting in the US

The US cities with the most Duchenne Muscular Dystrophy trials recruiting are Little Rock, Arkansas (7), Chicago, Illinois (5), Columbus, Ohio (5), Gainesville, Florida (5) and Nashville, Tennessee (5), counting trials with at least 1 open site in each city.

Hospitals that run trials for a rare condition often see more people with it than most clinics do, so this list can also help you find doctors who know Duchenne Muscular Dystrophy, even if no trial fits you.

Little Rock, Arkansas
7 trials recruiting
  • Arkansas Children's Hospital
  • Arkansas Childrens Hospital
Chicago, Illinois
5 trials recruiting
  • Ann & Robert H. Lurie Children's Hospital of Chicago
  • Lurie Children's Hospital of Chicago
  • Lurie Children's
Columbus, Ohio
5 trials recruiting
  • Nationwide Children's Hospital
  • Nationwide Children's
Gainesville, Florida
5 trials recruiting
  • University of Florida
  • University of Florida Clinical and Translational Research Building
  • University of Florida Clinical and Translational Science Institue
Nashville, Tennessee
5 trials recruiting
  • Vanderbilt University Medical Center
Sacramento, California
5 trials recruiting
  • University of California, Davis
  • UC Davis
  • UC Davis Health
Boston, Massachusetts
4 trials recruiting
  • Boston Children's Hospital
  • Massachusetts General Hospital
  • Brigham and Women's Hospital
Cincinnati, Ohio
4 trials recruiting
  • Cincinnati Children's Hospital Medical Center
  • University of Cincinnati

States with at least 1 open site: Arizona, Arkansas, California, Colorado, Connecticut, District of Columbia, Florida, Georgia, Illinois, Indiana, Iowa, Kansas, Massachusetts, Michigan, Minnesota, Missouri, New York, North Carolina, Ohio, Oregon, Pennsylvania, Tennessee, Texas, Utah, Virginia, Washington, Wisconsin.

Questions about finding a Duchenne Muscular Dystrophy trial near you

Are there Duchenne Muscular Dystrophy clinical trials near me?

As of October 12, 2026, 74 Duchenne Muscular Dystrophy clinical trials are recruiting or about to open (58 recruiting now, 16 opening soon). 29 of them have at least 1 open site in the United States, across 27 states. Enter your ZIP code on this page to rank every one of them by the distance to its closest open site, with the sites shown on a map.

Which states have Duchenne Muscular Dystrophy clinical trial sites?

As of October 12, 2026, recruiting Duchenne Muscular Dystrophy trials list open sites in 27 states. The US cities with the most Duchenne Muscular Dystrophy trials recruiting are Little Rock, Arkansas (7), Chicago, Illinois (5), Columbus, Ohio (5), Gainesville, Florida (5) and Nashville, Tennessee (5), counting trials with at least 1 open site in each city.

What if there is no Duchenne Muscular Dystrophy trial near me?

Some trials pay for or reimburse travel and lodging, and a few send staff or use local labs so fewer visits happen at the study site, so ask the study contact before ruling a trial out. You can also sign up on this page to get an email when a Duchenne Muscular Dystrophy trial opens a new site or changes status.

How is the distance to a trial site measured?

Distances are straight-line miles from the center of your ZIP code to each study site's listed location, not driving distance. Your browser looks up the ZIP code's coordinates with a free map service, Zippopotam.us, and the ZIP code is never sent to or stored by Trial Friend.

FDA-approved for Duchenne Muscular Dystrophy: Duvyzat (givinostat), Elevidys (delandistrogene moxeparvovec), Emflaza (deflazacort), Exondys 51 (eteplirsen), Vyondys 53 (golodirsen), Viltepso (viltolarsen), Amondys 45 (casimersen), Agamree (vamorolone).

Source: ClinicalTrials.gov, trials with status Recruiting or Not yet recruiting. Refreshed every 6 hours; counts as of October 12, 2026. Sites that ClinicalTrials.gov lists as closed or withdrawn are left out.