Also on Trial Friend:Spinal Muscular Atrophy pageCompare treatmentsMatch Me
All 52 Spinal Muscular Atrophy trials and their US sites
Enter your ZIP code above to sort them by how far their nearest open site is from you.
- Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)Most sites in California, Texas and VirginiaRecruitingNovartis Pharmaceuticals42US sites
25 states - Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular AtrophyMost sites in California, Pennsylvania and TexasRecruitingAges 3+Alcyone Therapeutics17US sites
12 states - A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular AtrophyMost sites in Texas, Arkansas and CaliforniaRecruitingPhase 2Ages 5-17argenx15US sites
14 states - A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular AtrophyMost sites in Texas, California and ArizonaRecruitingPhase 2Up to age 2Scholar Rock12US sites
8 states - A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)Most sites in California, Pennsylvania and VirginiaRecruitingPhase 1Ages 3+Biogen12US sites
9 states - ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)Most sites in Arkansas, California and MassachusettsRecruitingPhase 4Ages 2-100Novartis Pharmaceuticals6US sites
6 states - A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With RisdiplamMost sites in California, Massachusetts and VirginiaRecruitingPhase 3Ages 15-60Biogen3US sites
3 states - A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)Most sites in Illinois, Texas and VirginiaRecruitingPhase 3Ages 0 Days-42 DaysBiogen3US sites
3 states - A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their BabiesMost sites in California, Massachusetts and New YorkRecruitingAges 18-54Biogen3US sites
3 states - Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular DisordersMost sites in California, Massachusetts and New YorkRecruitingAges 5+Columbia University3US sites
3 states - A Registry of Cases of Spinal Muscular AtrophyOnly in TennesseeRecruitingSt. Jude Children's Research Hospital1US site
- A Study to Learn About the Safety and Effects of Salanersen (BIIB115) When Given to Babies With Spinal Muscular Atrophy (SMA) Who Were Previously Treated With Onasemnogene AbeparvovecOnly in TexasRecruitingPhase 3Ages 0 Days-7 MonthsBiogen1US site
- Characterizing Perceived Physical Fatigability in Nusinersen-treated SMAOnly in New YorkRecruitingAges 12+Columbia University1US site
- Clinical, Molecular and Imaging Biomarkers in Spinal and Bulbar Muscular Atrophy (SBMA)Only in MarylandRecruitingAges 18-120National Institute of Neurological Disorders and Stroke (NINDS)1US site
- Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed TherapiesOnly in TennesseeRecruitingAges 5-20St. Jude Children's Research Hospital1US site
- Gait and Bone Health in SMAOnly in New YorkRecruitingAges 8-50Jacqueline Montes1US site
- HABIT-ILE + FST in Children With SMA: Preliminary EffectivenessOnly in New YorkRecruitingAges 5-17Teachers College, Columbia University1US site
- A Head-to-head Study Comparing the Functional Value of Two Models of Robotically Assisted Rehabilitation in SMA (Spinal Muscular Atrophy) PatientsRecruitingUp to age 21Wiktor Dega University Orthopedic and Rehabilitation HospitalNo US site yet
- A Long-term Safety Study in Brazilian Patients With a Diagnosis of Spinal Muscular Atrophy Treated With ZolgensmaRecruitingAges 0-100Novartis PharmaceuticalsNo US site yet
- A Phase I/II Clinical Study to Evaluate SKG0201 Injection in Subjects With Spinal Muscular Atrophy Type IRecruitingPhase 1/2Up to age 180 DaysLanyue Biotech (Hangzhou) Co.No US site yet
New trials, status changes and new sites, straight from ClinicalTrials.gov. Unsubscribe anytime.
- Trial Alerts, when a new trial opens or a trial changes
- Disease Updates, FDA decisions and condition news, usually 1 or 2 emails a month
Who runs the Spinal Muscular Atrophy trials in the US, and what stage they are in
Of the 17 Spinal Muscular Atrophy trials with a US site, 3 are in Phase 3, the last stage before a company can ask the FDA for approval. Earlier Phase 1 or 2 tests of safety and dosing make up 3 of them. One is a Phase 4 study of an already approved treatment. The remaining 10 have no drug phase, such as studies that follow people over time or test a device or a way of giving care. Companies run 10 of them, and universities, hospitals, foundations and government groups run 7. The sponsors with the most are Biogen (5), Columbia University (2) and Novartis Pharmaceuticals (2). The most recently listed one first appeared on ClinicalTrials.gov on September 4, 2026.
Spinal Muscular Atrophy trials in the US, state by state
Of the 17 Spinal Muscular Atrophy trials with a US site, 15 accept children under 18. Their open sites are in 30 states, most often California, New York and Texas. A trial counts once in each state where it has an open site, and some trials accept both children and adults.
Show the other 20 states
US hospitals running the most Spinal Muscular Atrophy trials
Centers that run trials for a rare condition often see more people with it than most clinics do, so this list can also help you find doctors who know Spinal Muscular Atrophy.
- Boston Children's HospitalBoston, Massachusetts5 trials
- Columbia University Irving Medical CenterNew York, New York4 trials
- Neurology Rare Disease CenterFlower Mound, Texas4 trials
- Arkansas Children's HospitalLittle Rock, Arkansas3 trials
- Texas Children's HospitalHouston, Texas3 trials
- Ann & Robert H. Lurie Children's Hospital of ChicagoChicago, Illinois2 trials
- Children's Hospital ColoradoAurora, Colorado2 trials
- Childrens Hospital of the Kings Daughter NorfolkNorfolk, Virginia2 trials
- Phoenix Children's HospitalPhoenix, Arizona2 trials
- St. Jude Children's Research HospitalMemphis, Tennessee2 trials
Help getting to a Spinal Muscular Atrophy trial far from home
Ask the study team whether the trial pays back travel, parking and hotel costs, because many sponsors do. The FDA's guidance on paying research volunteers says paying back these costs does not count as pressuring someone to join.
These nonprofits also help patients reach care, and each one sets its own rules.
- Mercy Medical Angels
- Pays for gas cards, ground rides and airline tickets anywhere in the US, and it lists clinical trials as a reason to travel. Household income at or below 300% of the federal poverty guidelines, and usually a trip of 50 miles or more each way.
- Air Charity Network
- Volunteer pilots in all 50 states fly patients for free in small private planes, and members also fly people taking part in clinical trials. You must be able to walk and sit upright for the flight, show financial need and have a backup plan if weather cancels it.
- Ronald McDonald House
- Gives families a room near the hospital while a child gets care, through 394 House programs around the world. Families of a sick child, with rules set by each local chapter.
- Healthcare Hospitality Network
- Keeps a map of hospitality houses near hospitals, and most member houses charge little or nothing to patients and families. Each house sets its own rules, so check with the house near your study site.
Program details were checked on each program's website on October 24, 2026.
Questions about finding a Spinal Muscular Atrophy trial near you
Are there Spinal Muscular Atrophy clinical trials near me?
As of November 13, 2026, 52 Spinal Muscular Atrophy clinical trials are recruiting now and 9 are not yet recruiting. In the US, 17 of them have at least 1 open site, across 30 states. Enter your ZIP code on this page to rank every one of them by the distance to its closest open site, with the sites shown on a map.
Which states have Spinal Muscular Atrophy clinical trial sites?
Recruiting Spinal Muscular Atrophy trials list open sites in 30 states. California, New York and Massachusetts have the most, and the table on this page lists every state.
Are there Spinal Muscular Atrophy trials for children near me?
Of the 17 Spinal Muscular Atrophy trials with a US site, 15 accept children under 18. Their open sites are in 30 states, most often California, New York and Texas. Each trial sets its own age limits, so check the ages listed on a trial before you contact it.
Who pays for travel to a Spinal Muscular Atrophy clinical trial?
Many trial sponsors pay back travel, parking and hotel costs, so ask the study team before you rule out a far-away site. The FDA's guidance says paying back these costs does not count as pressuring someone to join. Charities such as Mercy Medical Angels and Air Charity Network can also help with rides and flights.
What if there is no Spinal Muscular Atrophy trial near me?
Some trials send staff to your home or use a local lab, so fewer visits happen at the study site. You can also sign up on this page to get an email when a Spinal Muscular Atrophy trial opens a new site or changes status.
How is the distance to a trial site measured?
Distances are straight-line miles from the center of your ZIP code to each study site's listed location, not driving distance. Your browser looks up the ZIP code's coordinates with a free map service, Zippopotam.us, and the ZIP code is never sent to or stored by Trial Friend.
FDA-approved for Spinal Muscular Atrophy: Evrysdi (risdiplam), Isembyld (apitegromab), Itvisma (onasemnogene abeparvovec-brve), Spinraza (nusinersen), Zolgensma (onasemnogene abeparvovec).
Clinical trials near you for related conditions
Source: ClinicalTrials.gov, trials with status Recruiting or Not yet recruiting. Refreshed every 6 hours; counts as of November 13, 2026. Sites that ClinicalTrials.gov lists as closed or withdrawn are left out. Children means the trial's age group includes people under 18.