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All 9 Achondroplasia trials and their US sites
Enter your ZIP code above to sort them by how far their nearest open site is from you.
- A Study of TYRA-300 in Children With Achondroplasia: BEACH301Most sites in Maryland, Missouri and TexasRecruitingPhase 2Ages 3-10Tyra Biosciences12US sites
9 states - Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With AchondroplasiaMost sites in Texas, California and DelawareRecruitingPhase 2/3Ages 2-17BioMarin Pharmaceutical9US sites
7 states - VIrtual STudy in Achondroplasia for the US (VISTA)Most sites in California, Maryland and North CarolinaRecruitingAges 0 Months-18BioMarin Pharmaceutical8US sites
7 states - A Clinical Trial to Evaluate Efficacy and Safety of TransCon CNP Compared With Placebo in Infants (0 to <2 Years of Age) With AchondroplasiaMost sites in Minnesota, Texas and WisconsinRecruitingPhase 2Ages 0-2Ascendis Pharma A/S3US sites
3 states - Interventional Study of Infigratinib in Children < 3 Years Old With Achondroplasia (ACH)Most sites in California, Maryland and WisconsinRecruitingPhase 2Ages 0-32 MonthsQED Therapeutics, a BridgeBio company3US sites
3 states - Achondroplasia Natural History Multicenter Clinical StudyOnly in MarylandRecruitingJohns Hopkins University1US site
- A Study in Children With AchondroplasiaRecruitingAges 30 Months-11Abbisko Therapeutics CoNo US site yet
- Prospective Longitudinal Multicentric Study to Measure Limb Movement in Patients With FGFR3-related Skeletal DysplasiaRecruitingAges 2-65SYSNAVNo US site yet
- Registry for Patients With Achondroplasia / Hypochondroplasia (OMPR-Ach/Hy)RecruitingFondazione IRCCS Ca' Granda, Ospedale Maggiore PoliclinicoNo US site yet
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Who runs the Achondroplasia trials in the US, and what stage they are in
Of the 6 Achondroplasia trials with a US site, 1 is in Phase 3, the last stage before a company can ask the FDA for approval. Earlier Phase 1 or 2 tests of safety and dosing make up 3 of them. The remaining 2 have no drug phase, such as studies that follow people over time or test a device or a way of giving care. Companies run 5 of them, and a university, hospital, foundation or government group runs the other. BioMarin Pharmaceutical runs the most, with 2. The most recently listed one first appeared on ClinicalTrials.gov on March 2, 2026.
Achondroplasia trials in the US, state by state
All 6 Achondroplasia trials with a US site accept children under 18. Their open sites are in 14 states, most often Maryland, California and Texas. A trial counts once in each state where it has an open site, and some trials accept both children and adults.
Show the other 4 states
US hospitals running the most Achondroplasia trials
Centers that run trials for a rare condition often see more people with it than most clinics do, so this list can also help you find doctors who know Achondroplasia.
- Johns Hopkins UniversityBaltimore, Maryland2 trials
- Ann & Robert H. Lurie Children's Hospital of ChicagoChicago, Illinois1 trial
- Baylor College of MedicineHouston, Texas1 trial
- Children's Hospital ColoradoAurora, Colorado1 trial
- Children's Hospital of PhiladelphiaPhiladelphia, Pennsylvania1 trial
- Children's Medical Center, DallasDallas, Texas1 trial
- Cincinnati Children's Hospital Medical CenterCincinnati, Ohio1 trial
- Consano Clinical Research, LLCSan Antonio, Texas1 trial
- Duke University HospitalDurham, North Carolina1 trial
- Johns Hopkins MedicineBaltimore, Maryland1 trial
Help getting to an Achondroplasia trial far from home
Ask the study team whether the trial pays back travel, parking and hotel costs, because many sponsors do. The FDA's guidance on paying research volunteers says paying back these costs does not count as pressuring someone to join.
These nonprofits also help patients reach care, and each one sets its own rules.
- Mercy Medical Angels
- Pays for gas cards, ground rides and airline tickets anywhere in the US, and it lists clinical trials as a reason to travel. Household income at or below 300% of the federal poverty guidelines, and usually a trip of 50 miles or more each way.
- Air Charity Network
- Volunteer pilots in all 50 states fly patients for free in small private planes, and members also fly people taking part in clinical trials. You must be able to walk and sit upright for the flight, show financial need and have a backup plan if weather cancels it.
- Ronald McDonald House
- Gives families a room near the hospital while a child gets care, through 394 House programs around the world. Families of a sick child, with rules set by each local chapter.
- Healthcare Hospitality Network
- Keeps a map of hospitality houses near hospitals, and most member houses charge little or nothing to patients and families. Each house sets its own rules, so check with the house near your study site.
Program details were checked on each program's website on October 24, 2026.
Questions about finding an Achondroplasia trial near you
Are there Achondroplasia clinical trials near me?
As of November 13, 2026, 9 Achondroplasia clinical trials are recruiting now and 2 are not yet recruiting. In the US, 6 of them have at least 1 open site, across 14 states. Enter your ZIP code on this page to rank every one of them by the distance to its closest open site, with the sites shown on a map.
Which states have Achondroplasia clinical trial sites?
Recruiting Achondroplasia trials list open sites in 14 states. Maryland, California and Texas have the most, and the table on this page lists every state.
Are there Achondroplasia trials for children near me?
All 6 Achondroplasia trials with a US site accept children under 18. Their open sites are in 14 states, most often Maryland, California and Texas. Each trial sets its own age limits, so check the ages listed on a trial before you contact it.
Who pays for travel to an Achondroplasia clinical trial?
Many trial sponsors pay back travel, parking and hotel costs, so ask the study team before you rule out a far-away site. The FDA's guidance says paying back these costs does not count as pressuring someone to join. Charities such as Mercy Medical Angels and Air Charity Network can also help with rides and flights.
What if there is no Achondroplasia trial near me?
Some trials send staff to your home or use a local lab, so fewer visits happen at the study site. You can also sign up on this page to get an email when an Achondroplasia trial opens a new site or changes status.
How is the distance to a trial site measured?
Distances are straight-line miles from the center of your ZIP code to each study site's listed location, not driving distance. Your browser looks up the ZIP code's coordinates with a free map service, Zippopotam.us, and the ZIP code is never sent to or stored by Trial Friend.
FDA-approved for Achondroplasia: Yuviwel (navepegritide), Voxzogo (vosoritide).
Clinical trials near you for related conditions
Source: ClinicalTrials.gov, trials with status Recruiting or Not yet recruiting. Refreshed every 6 hours; counts as of November 13, 2026. Sites that ClinicalTrials.gov lists as closed or withdrawn are left out. Children means the trial's age group includes people under 18.