Cystinosis Clinical Trials Near Me
As of October 12, 2026, 9 Cystinosis clinical trials are recruiting or about to open (7 recruiting now, 2 opening soon). 4 of them have at least 1 open site in the United States, across 7 states. Enter your ZIP code to see which are closest to you.
Also on Trial Friend:Cystinosis pageMatch Me
All 7 Cystinosis trials and their US sites
Enter your ZIP code above to sort them by how far their nearest open site is from you.
- DFT383 in Pediatric Participants With Nephropathic CystinosisPhoenix Children's Hospital (Recruiting Cohort 0 and 1), Phoenix, Arizona; University of California at San Diego - Rady Children's Hospital (Recruiting Cohort 0 and 1), San Diego, California; Stanford University - Stanford Children's Health (Recruiting Cohort 0 and 1), Stanford, California and 3 more sitesRecruitingPhase 1/2Ages 2 to 5Run by Novartis Pharmaceuticals
- Early Trial of Allogeneic Hematopoietic Stem Cell Transplantation for Patients Who Will Receive a Kidney Transplant From the Same DonorLucile Packard Children's Hospital, Palo Alto, CaliforniaRecruitingPhase 1/2Ages 1 to 30Run by Alice Bertaina
- Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at SanfordSanford Health, Sioux Falls, South DakotaRecruitingRun by Sanford Health
- Use of Cysteamine in the Treatment of CystinosisNational Institutes of Health Clinical Center, Bethesda, MarylandRecruitingAges 1 Week to 115Run by National Human Genome Research Institute (NHGRI)
- Cystinosis and Mitochondrial MetabolismNo open US site listed yetRecruitingAges 2+Run by Hospices Civils de Lyon
- European Cystinosis CohortNo open US site listed yetRecruitingRun by Institut National de la Santé Et de la Recherche Médicale, France
- National Registry of Rare Kidney DiseasesNo open US site listed yetRecruitingRun by UK Kidney Association
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Where Cystinosis trials are recruiting in the US
The US cities with the most Cystinosis trials recruiting are Atlanta, Georgia (1), Bethesda, Maryland (1), Houston, Texas (1), Palo Alto, California (1) and Philadelphia, Pennsylvania (1), counting trials with at least 1 open site in each city.
Hospitals that run trials for a rare condition often see more people with it than most clinics do, so this list can also help you find doctors who know Cystinosis, even if no trial fits you.
- Emory University School of Medicine - Children's Healthcare of Atlanta (recuiting Cohort 0)
- National Institutes of Health Clinical Center
- Baylor College of Medicine - Texas Children's Hospital (recuiting Cohort 0)
- Lucile Packard Children's Hospital
- Children's Hospital of Philadelphia (Recruiting Cohort 0 and 1)
- Phoenix Children's Hospital (Recruiting Cohort 0 and 1)
- University of California at San Diego - Rady Children's Hospital (Recruiting Cohort 0 and 1)
- Sanford Health
States with at least 1 open site: Arizona, California, Georgia, Maryland, Pennsylvania, South Dakota, Texas.
Questions about finding a Cystinosis trial near you
Are there Cystinosis clinical trials near me?
As of October 12, 2026, 9 Cystinosis clinical trials are recruiting or about to open (7 recruiting now, 2 opening soon). 4 of them have at least 1 open site in the United States, across 7 states. Enter your ZIP code on this page to rank every one of them by the distance to its closest open site, with the sites shown on a map.
Which states have Cystinosis clinical trial sites?
As of October 12, 2026, recruiting Cystinosis trials list open sites in Arizona, California, Georgia, Maryland, Pennsylvania, South Dakota and Texas.
What if there is no Cystinosis trial near me?
Some trials pay for or reimburse travel and lodging, and a few send staff or use local labs so fewer visits happen at the study site, so ask the study contact before ruling a trial out. You can also sign up on this page to get an email when a Cystinosis trial opens a new site or changes status.
How is the distance to a trial site measured?
Distances are straight-line miles from the center of your ZIP code to each study site's listed location, not driving distance. Your browser looks up the ZIP code's coordinates with a free map service, Zippopotam.us, and the ZIP code is never sent to or stored by Trial Friend.
FDA-approved for Cystinosis: Procysbi (cysteamine bitartrate delayed-release), Cystagon (cysteamine bitartrate), Cystaran (cysteamine hydrochloride ophthalmic solution 0.44%), Cystadrops (cysteamine ophthalmic solution 0.37%).
Source: ClinicalTrials.gov, trials with status Recruiting or Not yet recruiting. Refreshed every 6 hours; counts as of October 12, 2026. Sites that ClinicalTrials.gov lists as closed or withdrawn are left out.