Gaucher Disease Clinical Trials Near Me

As of November 13, 2026, 20 Gaucher Disease clinical trials are recruiting now and 8 are not yet recruiting. In the US, 12 of them have at least 1 open site, across 29 states and Washington, DC. Enter your ZIP code below to see which are closest to you.

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A study site. Select it to see its trials and get directions. Several sites close together. Select the number to zoom in.

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All 20 Gaucher Disease trials and their US sites

Enter your ZIP code above to sort them by how far their nearest open site is from you.

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Who runs the Gaucher Disease trials in the US, and what stage they are in

Of the 12 Gaucher Disease trials with a US site, 1 is in Phase 3, the last stage before a company can ask the FDA for approval. One more is an earlier Phase 1 or 2 test of safety and dosing. The remaining 10 have no drug phase, such as studies that follow people over time or test a device or a way of giving care. Companies run 3 of them, and universities, hospitals, foundations and government groups run 9. The sponsors with the most are University of Minnesota (3) and University of California, San Francisco (2). The most recently listed one first appeared on ClinicalTrials.gov on October 21, 2026.

Gaucher Disease trials in the US, state by state

Of the 12 Gaucher Disease trials with a US site, 6 accept children under 18. Their open sites are in 28 states and Washington, DC, most often California, Connecticut and Massachusetts. A trial counts once in each state where it has an open site, and some trials accept both children and adults.

StateTrialsChildrenAdultsCities with the most

Minnesota515Minneapolis (5)

California424San Francisco (4), Los Angeles (2), Beverly Hills (1), plus 3 more

New York313New York (3), Huntington (1), New Hyde Park (1), plus 3 more

North Carolina323Durham (3), Charlotte (1)

Pennsylvania323Pittsburgh (3), Philadelphia (2), Hershey (1)

Colorado212Aurora (2)

Connecticut222New Haven (2)

Georgia212Atlanta (1), Decatur (1)

Iowa212Iowa City (2)

Massachusetts222Boston (1), Lexington (1)

Show the other 20 states

New Jersey212Hackensack (2), Morristown (1), New Brunswick (1), plus 1 more

Ohio212Cincinnati (2), Cleveland (1), Columbus (1), plus 1 more

Virginia212Fairfax (2)

Arizona111Phoenix (1), Tucson (1)

Arkansas111Little Rock (1)

District of Columbia111Washington D.C. (1)

Florida111Coral Gables (1), Coral Springs (1), Jacksonville (1), plus 1 more

Illinois111Chicago (1)

Indiana111Indianapolis (1)

Maine111Portland (1)

Michigan111Ann Arbor (1), Detroit (1)

Missouri111Columbia (1), St Louis (1)

Nebraska111Omaha (1)

Oregon111Portland (1)

South Carolina111Greenville (1)

Tennessee111Nashville (1)

Texas101Dallas (1)

Utah111Salt Lake City (1)

Washington111Seattle (1), Tacoma (1)

Wisconsin111Milwaukee (1)

US hospitals running the most Gaucher Disease trials

Centers that run trials for a rare condition often see more people with it than most clinics do, so this list can also help you find doctors who know Gaucher Disease.

University of MinnesotaMinneapolis, Minnesota4 trials
Duke University Medical CenterDurham, North Carolina2 trials
UPMC Children's Hospital of PittsburghPittsburgh, Pennsylvania2 trials
Ann & Robert H. Lurie Children's Hospital of Chicago- Site Number : 840011Chicago, Illinois1 trial
Ann & Robert H. Lurie Children's Hospital of Chicago- Site Number : 840013Chicago, Illinois1 trial
Arkansas Children's Hospital- Site Number : 840109Little Rock, Arkansas1 trial
Atlantic Health System- Site Number : 840099Morristown, New Jersey1 trial
Atrium Health Carolinas Medical Center Hospital- Site Number : 840065Charlotte, North Carolina1 trial
Boston Children's Hospital- Site Number : 840092Boston, Massachusetts1 trial
Central ContactLexington, Massachusetts1 trial

Help getting to a Gaucher Disease trial far from home

Ask the study team whether the trial pays back travel, parking and hotel costs, because many sponsors do. The FDA's guidance on paying research volunteers says paying back these costs does not count as pressuring someone to join.

These nonprofits also help patients reach care, and each one sets its own rules.

Mercy Medical Angels: Pays for gas cards, ground rides and airline tickets anywhere in the US, and it lists clinical trials as a reason to travel. Household income at or below 300% of the federal poverty guidelines, and usually a trip of 50 miles or more each way.
Air Charity Network: Volunteer pilots in all 50 states fly patients for free in small private planes, and members also fly people taking part in clinical trials. You must be able to walk and sit upright for the flight, show financial need and have a backup plan if weather cancels it.
Ronald McDonald House: Gives families a room near the hospital while a child gets care, through 394 House programs around the world. Families of a sick child, with rules set by each local chapter.
Healthcare Hospitality Network: Keeps a map of hospitality houses near hospitals, and most member houses charge little or nothing to patients and families. Each house sets its own rules, so check with the house near your study site.

Program details were checked on each program's website on October 24, 2026.

Questions about finding a Gaucher Disease trial near you

Are there Gaucher Disease clinical trials near me?

Which states have Gaucher Disease clinical trial sites?

Recruiting Gaucher Disease trials list open sites in 29 states and Washington, DC. Minnesota, California and New York have the most, and the table on this page lists every state.

Are there Gaucher Disease trials for children near me?

Of the 12 Gaucher Disease trials with a US site, 6 accept children under 18. Their open sites are in 28 states and Washington, DC, most often California, Connecticut and Massachusetts. Each trial sets its own age limits, so check the ages listed on a trial before you contact it.

Who pays for travel to a Gaucher Disease clinical trial?

Many trial sponsors pay back travel, parking and hotel costs, so ask the study team before you rule out a far-away site. The FDA's guidance says paying back these costs does not count as pressuring someone to join. Charities such as Mercy Medical Angels and Air Charity Network can also help with rides and flights.

What if there is no Gaucher Disease trial near me?

Some trials send staff to your home or use a local lab, so fewer visits happen at the study site. You can also sign up on this page to get an email when a Gaucher Disease trial opens a new site or changes status.

How is the distance to a trial site measured?

Distances are straight-line miles from the center of your ZIP code to each study site's listed location, not driving distance. Your browser looks up the ZIP code's coordinates with a free map service, Zippopotam.us, and the ZIP code is never sent to or stored by Trial Friend.

FDA-approved for Gaucher Disease: Cerdelga (eliglustat), Cerezyme (imiglucerase), Elelyso (taliglucerase alfa), VPRIV (velaglucerase alfa), Zavesca (miglustat).

Source: ClinicalTrials.gov, trials with status Recruiting or Not yet recruiting. Refreshed every 6 hours; counts as of November 13, 2026. Sites that ClinicalTrials.gov lists as closed or withdrawn are left out. Children means the trial's age group includes people under 18.