Gaucher Disease Clinical Trials Near Me
As of October 12, 2026, 25 Gaucher Disease clinical trials are recruiting or about to open (19 recruiting now, 6 opening soon). 11 of them have at least 1 open site in the United States, across 31 states. Enter your ZIP code to see which are closest to you.
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All 19 Gaucher Disease trials and their US sites
Enter your ZIP code above to sort them by how far their nearest open site is from you.
- International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registryPhoenix Children's Hospital- Site Number : 840003, Phoenix, Arizona; University of Arizona- Site Number : 840015, Tucson, Arizona; Arkansas Children's Hospital- Site Number : 840109, Little Rock, Arkansas and 67 more sitesRecruitingRun by Genzyme, a Sanofi Company
- A Gaucher Disease Gene Therapy Trial With FLT201Kaiser Permanente - CA, Los Angeles, California; UCLA Health, Los Angeles, California; University of California, San Francisco (UCSF), San Francisco, California and 13 more sitesRecruitingPhase 3Ages 18+Run by Spur Therapeutics
- A Long-term Follow-up Study of Gaucher DiseaseDuke University Medical Center, Durham, North CarolinaRecruitingRun by Duke University
- Advancing Integrated Therapies for Gaucher DiseaseYale New Haven Health System, New Haven, ConnecticutRecruitingAges 3 Months to 75Run by Yale University
- Extracellular Vesicles as Potential Biomarkers and Therapeutic Target in Gaucher DiseaseUniversity of Minnesota, Minneapolis, MinnesotaRecruitingAges 18 to 80Run by University of Minnesota
- Gaucher Disease Outcome Survey (GOS)Central Contact, Lexington, MassachusettsRecruitingRun by Shire
- Longitudinal Study of Neurodegenerative DisordersUPMC Children's Hospital of Pittsburgh, Pittsburgh, PennsylvaniaRecruitingRun by University of Pittsburgh
- MAGNETIC RESONANCE SPECTROSCOPY BIOMARKERS IN TYPE 3 GAUCHER DISEASE (GD3)University of Minnesota, Minneapolis, MinnesotaRecruitingAges 18 to 80Run by University of Minnesota
- Oxidative Stress and Inflammatory Biomarkers in Gaucher DiseaseUniversity of Minnesota, Minneapolis, MinnesotaRecruitingAges 18 to 75Run by University of Minnesota
- PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)University of California, San Francisco, CaliforniaRecruitingPhase 1Ages 18 to 50Run by University of California, San Francisco
- Registry of Patients Diagnosed With Lysosomal Storage DiseasesUniversity of California San Francisco, San Francisco, CaliforniaRecruitingUp to age 64Run by University of California, San Francisco
- A Clinical Study Evaluating LY-M001 Injection in the Treatment of Adult Patients With Type I Gaucher DiseaseNo open US site listed yetRecruitingPhase 1/2Ages 18 to 60Run by Lingyi Biotech Co., Ltd.
- A Study of the Safety and Preliminary Efficacy of LY-M001 Injection in the Treatment of Adult Patients With Gaucher Disease Type INo open US site listed yetRecruitingAges 18 to 60Run by He Huang
- An Exploratory Clinical Trial of VGN-R08b in Patients With Type II Gaucher DiseaseNo open US site listed yetRecruitingEarly Phase 1Ages 0 Months to 24 MonthsRun by Xinhua Hospital, Shanghai Jiao Tong University School of Medicine
- GammaGA: Prevalence of Acid Sphingomyelinase Deficiency Disease (ASMD) and Gaucher Disease in Patients With Monoclonal Gammopathies and/or Multiple MyelomaNo open US site listed yetRecruitingAges 18 to 99Run by Fundación Española de Hematología y Hemoterapía
- Gaucherite - A Study to Stratify Gaucher DiseaseNo open US site listed yetRecruitingRun by Cambridge University Hospitals NHS Foundation Trust
- Institutional Registry of Rare DiseasesNo open US site listed yetRecruitingRun by Hospital Italiano de Buenos Aires
- Prodromal Parkinsonian Features in GBA1 Mutation CarriersNo open US site listed yetRecruitingAges 40 to 75Run by Shaare Zedek Medical Center
- World Data on Ambroxol for Patients With GD and GBA Related PDNo open US site listed yetRecruitingUp to age 100Run by Shaare Zedek Medical Center
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Where Gaucher Disease trials are recruiting in the US
The US cities with the most Gaucher Disease trials recruiting are Minneapolis, Minnesota (5), San Francisco, California (4), Durham, North Carolina (3), Pittsburgh, Pennsylvania (3) and Cincinnati, Ohio (2), counting trials with at least 1 open site in each city.
Hospitals that run trials for a rare condition often see more people with it than most clinics do, so this list can also help you find doctors who know Gaucher Disease, even if no trial fits you.
- University of Minnesota
- Children's Hospitals and Clinics of Minnesota- Site Number : 840046
- Children's Hospitals and Clinics of Minnesota- Site Number : 840114
- and 1 more
- University of California
- University of California San Francisco
- University of California San Francisco - Parnassus Campus- Site Number : 840051
- and 1 more
- Duke University Medical Center
- Duke University Medical Center Genetics Dept- Site Number : 840037
- UPMC Children's Hospital of Pittsburgh
- UPMC Children's Hospital of Pittsburgh- Site Number : 840023
- Cincinnati Children's Hospital Medical Center
- Cincinnati Children's Hospital Medical Center- Site Number : 840026
- Lysosomal Rare Disorders Research and Treatment Center
- O & O Alpan- Site Number : 840025
- Hackensack University Medical Center
- Joseph M. Sanzari Children's Hospital- Site Number : 840101
- University of Iowa Health Care
- University of Iowa- Site Number : 840032
States with at least 1 open site: Arizona, Arkansas, California, Colorado, Connecticut, District of Columbia, Florida, Georgia, Illinois, Indiana, Iowa, Maine, Massachusetts, Michigan, Minnesota, Missouri, Nebraska, Nevada, New Jersey, New York, North Carolina, Ohio, Oregon, Pennsylvania, South Carolina, Tennessee, Texas, Utah, Virginia, Washington, Wisconsin.
Questions about finding a Gaucher Disease trial near you
Are there Gaucher Disease clinical trials near me?
As of October 12, 2026, 25 Gaucher Disease clinical trials are recruiting or about to open (19 recruiting now, 6 opening soon). 11 of them have at least 1 open site in the United States, across 31 states. Enter your ZIP code on this page to rank every one of them by the distance to its closest open site, with the sites shown on a map.
Which states have Gaucher Disease clinical trial sites?
As of October 12, 2026, recruiting Gaucher Disease trials list open sites in 31 states. The US cities with the most Gaucher Disease trials recruiting are Minneapolis, Minnesota (5), San Francisco, California (4), Durham, North Carolina (3), Pittsburgh, Pennsylvania (3) and Cincinnati, Ohio (2), counting trials with at least 1 open site in each city.
What if there is no Gaucher Disease trial near me?
Some trials pay for or reimburse travel and lodging, and a few send staff or use local labs so fewer visits happen at the study site, so ask the study contact before ruling a trial out. You can also sign up on this page to get an email when a Gaucher Disease trial opens a new site or changes status.
How is the distance to a trial site measured?
Distances are straight-line miles from the center of your ZIP code to each study site's listed location, not driving distance. Your browser looks up the ZIP code's coordinates with a free map service, Zippopotam.us, and the ZIP code is never sent to or stored by Trial Friend.
FDA-approved for Gaucher Disease: Cerdelga (eliglustat), Cerezyme (imiglucerase), Elelyso (taliglucerase alfa), Zavesca (miglustat), VPRIV (velaglucerase alfa).
Source: ClinicalTrials.gov, trials with status Recruiting or Not yet recruiting. Refreshed every 6 hours; counts as of October 12, 2026. Sites that ClinicalTrials.gov lists as closed or withdrawn are left out.