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All 4 Leber Congenital Amaurosis trials and their US sites
Enter your ZIP code above to sort them by how far their nearest open site is from you.
- Safety and Tolerability of Subretinal OPGx-RDH12-1001 for LCA-Associated Inherited Retinal Degeneration (LCA-IRD)Most sites in Texas, Arizona and PennsylvaniaRecruitingPhase 1/2Ages 18+Opus Genetics4US sites
3 states - Study to Evaluate Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION)Most sites in California, Florida and IowaRecruitingPhase 3Ages 6+Laboratoires Thea4US sites
4 states - Inherited Retinal Degenerative Disease RegistryOnly in MarylandRecruitingFoundation Fighting Blindness1US site
- Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at SanfordOnly in South DakotaRecruitingSanford Health1US site
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Who runs the Leber Congenital Amaurosis trials in the US, and what stage they are in
Of the 4 Leber Congenital Amaurosis trials with a US site, 1 is in Phase 3, the last stage before a company can ask the FDA for approval. One more is an earlier Phase 1 or 2 test of safety and dosing. The remaining 2 have no drug phase, such as studies that follow people over time or test a device or a way of giving care. Companies run 2 of them, and universities, hospitals, foundations and government groups run 2. The most recently listed one first appeared on ClinicalTrials.gov on July 2, 2026.
Leber Congenital Amaurosis trials in the US, state by state
Of the 4 Leber Congenital Amaurosis trials with a US site, 3 accept children under 18. Their open sites are in 6 states, most often California, Florida and Iowa. A trial counts once in each state where it has an open site, and some trials accept both children and adults.
US hospitals running the most Leber Congenital Amaurosis trials
Centers that run trials for a rare condition often see more people with it than most clinics do, so this list can also help you find doctors who know Leber Congenital Amaurosis.
- Associated Retina ConsultantsPhoenix, Arizona1 trial
- Foundation Fighting BlindnessColumbia, Maryland1 trial
- Perelman School of Medicine, University of PennsylvaniaPhiladelphia, Pennsylvania1 trial
- Retina Consultants of Texas & Retina Group Inc.Houston, Texas1 trial
- Retina Foundation of the SouthwestDallas, Texas1 trial
- Sanford HealthSioux Falls, South Dakota1 trial
- UCSF Wayne and Gladys Valley Center for VisionSan Francisco, California1 trial
- University of IowaIowa City, Iowa1 trial
- University of Miami - Bascom Palmer Eye InstituteMiami, Florida1 trial
- University of Pennsylvania - Center for Advanced Retinal & Ocular TherapeuticsPhiladelphia, Pennsylvania1 trial
Help getting to a Leber Congenital Amaurosis trial far from home
Ask the study team whether the trial pays back travel, parking and hotel costs, because many sponsors do. The FDA's guidance on paying research volunteers says paying back these costs does not count as pressuring someone to join.
These nonprofits also help patients reach care, and each one sets its own rules.
- Mercy Medical Angels
- Pays for gas cards, ground rides and airline tickets anywhere in the US, and it lists clinical trials as a reason to travel. Household income at or below 300% of the federal poverty guidelines, and usually a trip of 50 miles or more each way.
- Air Charity Network
- Volunteer pilots in all 50 states fly patients for free in small private planes, and members also fly people taking part in clinical trials. You must be able to walk and sit upright for the flight, show financial need and have a backup plan if weather cancels it.
- Ronald McDonald House
- Gives families a room near the hospital while a child gets care, through 394 House programs around the world. Families of a sick child, with rules set by each local chapter.
- Healthcare Hospitality Network
- Keeps a map of hospitality houses near hospitals, and most member houses charge little or nothing to patients and families. Each house sets its own rules, so check with the house near your study site.
Program details were checked on each program's website on October 24, 2026.
Questions about finding a Leber Congenital Amaurosis trial near you
Are there Leber Congenital Amaurosis clinical trials near me?
As of November 13, 2026, 4 Leber Congenital Amaurosis clinical trials are recruiting now and 1 is not yet recruiting. In the US, 4 of them have at least 1 open site, across 8 states. Enter your ZIP code on this page to rank every one of them by the distance to its closest open site, with the sites shown on a map.
Which states have Leber Congenital Amaurosis clinical trial sites?
Recruiting Leber Congenital Amaurosis trials list open sites in Arizona, California, Florida, Iowa, Maryland, Pennsylvania, South Dakota and Texas.
Are there Leber Congenital Amaurosis trials for children near me?
Of the 4 Leber Congenital Amaurosis trials with a US site, 3 accept children under 18. Their open sites are in 6 states, most often California, Florida and Iowa. Each trial sets its own age limits, so check the ages listed on a trial before you contact it.
Who pays for travel to a Leber Congenital Amaurosis clinical trial?
Many trial sponsors pay back travel, parking and hotel costs, so ask the study team before you rule out a far-away site. The FDA's guidance says paying back these costs does not count as pressuring someone to join. Charities such as Mercy Medical Angels and Air Charity Network can also help with rides and flights.
What if there is no Leber Congenital Amaurosis trial near me?
Some trials send staff to your home or use a local lab, so fewer visits happen at the study site. You can also sign up on this page to get an email when a Leber Congenital Amaurosis trial opens a new site or changes status.
How is the distance to a trial site measured?
Distances are straight-line miles from the center of your ZIP code to each study site's listed location, not driving distance. Your browser looks up the ZIP code's coordinates with a free map service, Zippopotam.us, and the ZIP code is never sent to or stored by Trial Friend.
FDA-approved for Leber Congenital Amaurosis: Luxturna (voretigene neparvovec-rzyl).
Clinical trials near you for related conditions
Source: ClinicalTrials.gov, trials with status Recruiting or Not yet recruiting. Refreshed every 6 hours; counts as of November 13, 2026. Sites that ClinicalTrials.gov lists as closed or withdrawn are left out. Children means the trial's age group includes people under 18.