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Medical genetics
2 conditions and 4 prescribing guides so far.
By specialty and condition
Each condition page compares its drugs side by side and lists FDA decisions, label changes and open trials.
Prescribing guides
The first 90 days from the prescriber's side, built from the current label, the drugmaker's program and one public insurer policy.
Fabry disease
Elfabrio (pegunigalsidase alfa-iwxj)Dosing, Infusion Rates and PA CriteriaNo REMS. Prior authorization, Elfabrio Start Form, a site with CPR-capable medical support for initial infusions, and premedication planned case by case.Fabrazyme (agalsidase beta)Dosing, Infusion Rate and PA CriteriaNo REMS. Boxed warning: initiate in a healthcare setting with monitoring and CPR equipment. Prior authorization and a site of care before the first infusion.Galafold (migalastat)Amenability, Dosing and PA CriteriaNo REMS; Galafold Referral Form (also a prescription in some states) with patient consent to Amicus Assist by fax 1-833-264-2873 or email assist@amicusrx.com; specialty pharmacy ships after any prior authorization.Gaucher disease
Cerezyme (imiglucerase)Dosing, Infusion Volumes, PA CriteriaNo REMS. Boxed warning: initiate in a healthcare setting with monitoring and CPR equipment. Prior authorization and a site of care before the first infusion.